Search for Clinical Trial Results
Mucopolysaccharidosis III - 25 Studies Found
Status | Study |
Recruiting |
Study Name: Biomarker for Sanfilippo Disease Condition:
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Enrolling by invitation |
Study Name: An Extension Study to Determine Safety and Efficacy for Pediatric Patients With MPS Type IIIA Disease Who Participated in Study HGT-SAN-093. Condition:
Date: 2015-01-21 Interventions: Drug: HGT-1410 HGT-1410 administered according to Patient Group assignment. |
Recruiting |
Study Name: A Treatment Study of Mucopolysaccharidosis Type IIIB Condition:
Date: 2016-02-27 Interventions: Drug: BMN 250 Chimeric fusion of recombinant human alpha-N-acetylglucosaminidase and truncated human ins |
Completed |
Study Name: Neurobehavioral Phenotypes in MPS III Condition:
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Completed |
Study Name: Evaluation of Blood Brain Barrier Integrity and Structural Abnormalities in MPS IIIB Patients Using Multimodal Magnetic Resonance Imaging Condition: MPS IIIB (Sanfilippo B Syndrome) Date: 2014-03-12 |
Recruiting |
Study Name: A Study of Mucopolysaccharidosis Type IIIB (MPS IIIB) Condition:
Interventions: Other: This is an observational study This is an observational study |